How to be an ally to those of us with sickle cell disease Sickle cell disease is highly misunderstood, and our patient community is acutely aware of this. One of the key lessons I’ve …

7 hours ago · With the addition of Casgevy, Children’s Hospital Los Angeles now offers two gene therapies for sickle cell, the first being Lyfgenia.

2 days ago · The first patient has been enrolled in a Phase 1 trial by the NHLBI that's evaluating fostamatinib as a treatment for sickle cell disease.

Read about the prognosis for adults and children with sickle cell anemia, a disease marked by deformed red blood cells and acute pain crises.

6 days ago · Columnist Mary Shaniqua explains how to be an ally to the sickle cell community, and why that kind of support is essential for patients.

SCD patients free of VOEs after treatment with gene-editing therapy Nearly all the patients with severe sickle cell disease (SCD) who were treated with renizgamglogene autogedtemcel (reni …

Dec 8, 2023 · The FDA approved Lyfgenia, a gene therapy from Bluebird Bio known as lovo-cel, for SCD patients, 12 and older, with a history of painful VOCs.

Sickle Cell Disease News is a digital platform intended to provide the sickle cell disease (SCD) community with the most recent news and information on SCD, as well as first-hand …

Nov 7, 2024 · BEAM-101, a gene-editing stem cell therapy, showed early signs of efficacy among the first treated sickle cell patients in a clinical trial.

Dec 19, 2024 · The treatment also increased total hemoglobin levels and was well tolerated, according to a company press release from Editas Medicine, the developer of the gene-editing …