Shares of Tempest Therapeutics (TPST) ended higher on Wednesday amid a broader market rebound on the U.S. pausing tariffs and ...

Since the Orphan Drug Act went into effect in 1983, more than 600 drugs have been approved for rare diseases, according to ...

近日，血霁生物自主研发的“全球新”Fisrt-in-Class细胞治疗产品XJ-MK-002治疗巨大血小板综合征 （BSS）获得美国食品药品监督管理局 （FDA）认证授予孤儿药 （Orphan Drug Designation，ODD）资格。这是XJ ...

EMA orphan drug designation is awarded to drugs intended to treat rare diseases that are life-threatening or chronically ...

Results from Phase II studies demonstrated that rilzabrutinib showed clinically meaningful outcomes in patients with warm ...

AscellaHealth has announced its role as a Silver Sponsor of the World Orphan Drug Congress USA (WODC), which will convene ...

Avidity Biosciences, Inc. (Nasdaq: RNA), a biopharmaceutical company committed to delivering a new class of RNA therapeutics called Antibody Oligonucleotide Conjugates (AOCs™), today announced that ...

FDA grants orphan drug designation to HLX22 for gastric cancer, with a phase 2 trial showing improved progression-free ...

The FDA has granted orphan drug designation to rilzabrutinib for IgG4-related disease and warm autoimmune hemolytic anemia, ...

About IgG4-RD IgG4-RD affects approximatively eight out of 100,000 adult patients in the US each year and is a rare, progressive, relapsing, chronic fibro-inflammatory condition which can manifest in ...

AscellaHealth, a global partner delivering customizable solutions to support the specialty pharmaceutical industry, proudly announces its role as a Silver Sponsor at the World Orphan Drug Congress USA ...

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