Researchers at Tohoku University have discovered that an oral drug called MA-5 can improve both heart and muscle problems in Barth syndrome, a rare genetic disorder affecting 1 in 300,000 births ...

The Barth Syndrome Treatment Market represents a critical segment within the rare disease therapeutic landscape, addressing the urgent medical needs of patients affected by this life-threatening ...

Researchers at Tohoku University have discovered that an oral drug called MA-5 can improve both heart and muscle problems in Barth syndrome, a rare genetic disorder affecting 1 in 300,000 ...

MA-5, an oral drug for Barth syndrome, could improve heart and muscle function by restoring energy production. Clinical trials are now underway.

Researchers at Tohoku University have discovered that an oral drug called MA-5 can improve both heart and muscle problems in Barth syndrome, a rare genetic disorder affecting 1 in 300,000 births ...

SAN FRANCISCO (KPIX) -- With the FDA recently rejecting a drug application that aims to help those living with Barth Syndrome, one Bay Area family is frustrated by the delay of approved treatments ...

Approximately 150 people live with Barth Syndrome nationwide, an ultra-rare genetic disorder that affects only males and impacts muscle and heart muscle health.