Metagenomi is now working on preclinical studies to advance MGX-001, its experimental gene-editing therapy for hemophilia A, with the goal of bringing the treatment candidate into clinical trials in ...

Gene editing stands for the methods to precisely make changes to a specific nucleic acid sequence. With the recent development of the clustered regularly interspaced short palindromic repeats (CRISPR) ...

In this installment of Rebelliously Curious, we delve into one of the most debated scientific advancements of our time: CRISPR gene-editing technology. Joining us is Neal Baer, M.D.—pediatrician, ...

These unique, branched molecules help LNPs break through the endosomal membrane, making them more effective at delivering mRNA and gene-editing tools. In a recent study in Nature Communications ...

However, gene editing is banned. Likewise, the British Horseracing Authority has banned any "gene therapy or cellular manipulation" that could give an animal an advantage, said The Times.

Fate Therapeutics uses iPSC and gene editing to offer scalable off-the-shelf therapies. Read more to see why I rate FATE ...

It is of value to know at the onset of a project whether the transgenes or gene editing reagents are functioning as predicted. To test molecular reagents transiently, we implemented an improved, ...

Key criticisms of the article include the current inaccuracy of gene-editing technologies, the challenges in accurately identifying causal gene variants, and the possibility of pleiotropic effects ...

DURHAM, N.C.--(BUSINESS WIRE)--Precision BioSciences, Inc. (Nasdaq: DTIL), a clinical stage gene editing company utilizing its novel proprietary ARCUS ® platform to develop in vivo gene editing ...

Bengaluru (Karnataka) [India], January 16: Bengaluru-based biotechnology startup, CrisprBits Private Limited, has inaugurated a CRISPR gene editing and diagnostics laboratory in Bengaluru. The new ...

Gene therapy has progressed to a compelling therapeutic approach for various neurodegenerative disorders. Several efforts to enhance gene therapy rely on discovering novel vectors, recent curative ...