However, the central nervous system-focused company is also planning to submit a request with the FDA next year to take ETX201, its AAV9-based vectorized microRNA (miRNA) therapy for Angelman ...

This review synthesizes current advancements in understanding miRNA-mediated immune regulation in DCM. We highlight the need for further research to elucidate the complex interactions between ...

The therapy increases the amount of blood the ... They showed that shutting down a damaged copy of a gene called a microRNA (miRNA) enabled ... Novel Genome Editing Approach Restores Hearing ...

A recently published study by the the Western Ontario Registry for Early OA (WOREO) Knee Study team suggests that while synovitis increases in OA, the exhaustion and dysfunction of immune-regulatory ...

The goal of therapy is to rework our stories in a way that is helpful and meaningful to us.